Iwagawa T, Masumoto H, Tabuchi H, Tani K, Conklin BR, Watanabe S. Evaluation of CRISPR/Cas9 exon-skipping vector for choroideremia using human induced pluripotent stem cell-derived RPE. J Gene Med. 2023 Feb; 25(2):e3464.
Iwagawa T, Masumoto H, Tabuchi H, Tani K, Conklin BR, Watanabe S